New life saving medicines

11 April 2023 - The Australian Government has added the two medicines, Kanuma (sebelipase alfa) and Cerdelga (eliglustat) to the Life ...

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Rare cancer sufferers fight to get drugs on PBS

9 September 2022 - People with rare cancers are being forced to sell their homes, raid their superannuation and fundraise ...

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Australia among world's best in treating debilitating and often fatal muscle disorder

4 September - Australia has become one of the first countries in the world to fund a new, next-generation treatment ...

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Mirum Pharmaceuticals broadens Expanded Access Program for maralixibat in Alagille syndrome to Europe and Australia

5 November 2020 - Maralixibat Expanded Access Program now available for patients with pruritus associated with Alagille syndrome in Australia and ...

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Cystic fibrosis is the reason for denial of Irish man's re-entry visa by Australian Government, family says

26 February 2020 - A young Irish man with cystic fibrosis who calls Western Australia home has been denied entry ...

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First National Action Plan for rare diseases

26 February 2020 - The Australian Government will provide up to $3.3 million for activities to implement the first National Strategic ...

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Perth boy battles cystic fibrosis, with a life extending drug frustratingly out of reach

15 July 2019 - In many ways Connor Barrett is just like any other kid - he loves Peppa Pig ...

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Irish cystic fibrosis family face €12,400 bill after deportation victory in Australia

15 July 2019 - An Irish family threatened with deportation from Australia because their son has cystic fibrosis have been ...

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Family faces deportation from Australia after son diagnosed with cystic fibrosis

10 April 2019 - Anthony and Christine Hyde's application for permanent residence in Australia has been rejected - because of their ...

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Migalastat (Galafold) included on the Life Saving Drugs Program

1 November 2018 - Galafold is an oral treatment that has been included on the Life Saving Drugs Program to treat ...

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Medicine for rare disease made free on the Life Saving Drugs Program

1 November 2018 - The Australian Government has made a new medicine available for free for an extremely rare and potentially ...

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Patients with rare disease get free access to life-saving wonder drug

1 November 2018 - Australians with a rare genetic condition, that can kill sufferers in the most severe cases by ...

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Mum's battle for life-saving drug

12 October 2018 - At just 29 years of age, doting mother Kate McKenzie has faced more battles than anyone ...

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Battle for wonder drug pays off

13 September 2018 - A West Pymble mother feels the “weight of the world” has been lifted following the federal ...

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Vertex announces reimbursement agreement in Australia for Orkambi (lumacaftor/ivacaftor) for people with cystic fibrosis ages six years and older with two copies of the F508del mutation

3 September 2018 - Approximately 1,300 patients in Australia join the thousands of patients worldwide who already have access to lumacaftor/ivacaftor. ...

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