Posted by Michael Wonder on 17 Feb 2023
UK’s most expensive drug Libmeldy saved Teddi Shaw, but is too late for her sister
16 February 2023 - A toddler with a rare inherited condition has become the first child to be treated by the NHS with a new life-saving gene therapy.
Teddi Shaw was diagnosed in time because her older sister Nala showed symptoms - but it was too late to treat Nala, who is now terminally ill.
Both girls have MLD, which severely damages the brain and nervous system.
