28 February 2022 - England's Rare Disease Action plan is published today with details of how to improve diagnosis, care and treatment of people with rare diseases in England.
“Nearly 40% of the medicines now in development are for rare or very rare conditions, including many cell and gene therapies, so we very much welcome the commitments to help people get rapid access to them. We would urge all action plan delivery partners to work together, with industry, to make these plans a reality."