Posted by Michael Wonder on 08 Dec 2015
FDA approves first drug to treat a rare enzyme disorder in pediatric and adult patients
8 December 2015 - Today, the U.S. FDA approved Kanuma (sebelipase alfa) as the first treatment for patients with a rare disease known as lysosomal acid lipase deficiency.
For more details, go to: http://www.fda.gov/NewsEvents/Newsroom/PressAnnouncements/ucm476013.htm?source=govdelivery&utm_medium=email&utm_source=govdelivery
