MHRA approves first UK treatment for congenital thrombotic thrombocytopenic purpura

UK Government

12 May 2025 - The MHRA has today approved rADAMTS13 (Adzynma), the first UK treatment to treat congenital thrombotic thrombocytopenic purpura in patients of all ages.

This medicine has been approved through the International Recognition Procedure (IRP). The IRP allows the MHRA to take into account the expertise and decision-making of trusted regulatory partners for the benefit of UK patients.

Read UK Government press release

Michael Wonder

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Michael Wonder

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Outcome , Medicine , Registration , UK