Posted by Michael Wonder on 09 Jan 2024
Orphan drug label expansions: analysis of subsequent rare and common indication approvals
8 January 2024 - We found that 491 novel orphan drugs were approved between 1990 and 2022.
To date, 65% have been approved for a single rare disease, 15% have been approved for multiple rare diseases, and 20% have been approved for both rare and common diseases.
