Posted by Michael Wonder on 31 Oct 2018
Patients with rare disease get free access to life-saving wonder drug
1 November 2018 - Australians with a rare genetic condition, that can kill sufferers in the most severe cases by the age of 50, will now have free access to a next-generation medication that usually costs hundreds of thousands of dollars a year.
Health Minister Greg Hunt will on Thursday announce Galafold (migalastat) has been added to the federal government’s Life Saving Drugs Program for the treatment of Fabry disease.
Lea Chant, 55, has taken Galafold as a clinical trial participant for the past eight years.
She and her son Christopher were diagnosed with Fabry disease and the same mutation when Christopher was six-months-old.
