Posted by Michael Wonder on 19 Apr 2018
Price tag for newly approved Crysvita is "responsible," says PBM Express Scripts
18 April 2018 - Taking the rebates that it expects to negotiate into consideration, Ultragenyx said that burosumab will cost approximately $160,000 per patient per year for children and $200,000 per patient per year for adults, depending on body weight.
The FDA has approved Ultragenyx and Kyowa Hakko Kirin’s burosumab-twza (Crysvita) for the treatment of X-linked hypophosphatemia (XLH) in adult and pediatric patients aged 1 year or older.
Steven B. Miller, MD, chief medical officer of pharmacy benefit manager (PBM) Express Scripts, told Forbes that “It’s not inexpensive, but I do believe the right word is responsible,” and added that the cost of the drug is “going to be a very reasonable tradeoff” considering the surgical interventions that patients currently require for XLH. By comparison, said Miller, other genetic diseases that cause similar levels of disability have treatments that cost $600,000 or more per year.
