30 January 2024 - NICE is unable to make a recommendation on the use of treosulphan (Trecondi) in combination with fludarabine phosphate before allogeneic stem cell transplantation for babies, children and young people aged 1 month to 17 years with a non-malignant disease.
This is because Medac Pharma did not provide an evidence submission. NICE will review this decision if Medac Pharma decides to make a submission.