More children now eligible for cystic fibrosis drug

18 July 2022 - Effective today, the Province will pay for the cystic fibrosis drug Trikafta for children aged six to ...

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Alberta expands access to cystic fibrosis drug Trikafta for children 6 to 11

11 July 2022 - Children with cystic fibrosis can now live 'longer, healthier and fuller lives,' says advocate. ...

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Budget 2022: two year old girl and mum travel to Wellington in hopes of getting funding for devastating spinal illness

19 May 2022 - Dozens of people are travelling to Wellington for the Budget to highlight concerns about sick children ...

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NICE recommends Koselugo for the treatment of neurofibromatosis type 1

8 April 2022 - NICE has recommended AstraZeneca and MSD’s Koselugo (selumetinib) for use by the NHS in England, within ...

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Atidarsagene autotemcel for treating metachromatic leukodystrophy

28 March 2022 - NICE has published evidence-based recommendations on atidarsagene autotemcel (Libmeldy) for treating metachromatic leukodystrophy in children. ...

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Eligible Australian kids 16+ can now get a booster

3 February 2022 - From today, eligible Australians aged 16 and 17 years old will be able to receive a COVID-19 ...

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Health technology assessment of paediatric medicines: European landscape, challenges and opportunities inside the conect4children project

28 January 2022 - This article aims at describing the most relevant elements of the drug development process in the paediatric ...

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How are child specific utility instruments used in decision making in Australia? A review of Pharmaceutical Benefits Advisory Committee public summary documents.

28 January 2022 - Measuring and valuing health-related quality of life in children can be challenging but is an important component ...

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Immunotherapy with blinatumomab improves the chances of survival in very rare childhood blood cancer

20 January 2022 - The Federal Joint Committee (G-BA) today classified the additional benefit of the active ingredient blinatumomab as significant ...

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Children and young people set to benefit from new treatment for peanut allergy

23 December 2021 - Children and young people aged between 4 and 17 with a peanut allergy could be set to ...

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NICE terminates appraisal of new treatment for adolescents with obesity

1 December 2021 - NICE is unable to make a recommendation on liraglutide (Saxenda) for managing obesity in adolescents aged 12 ...

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Audrey Ashman’s bone treatment for rare genetic disease known as XLH denied government subsidy

24 October 2021 - Audrey Ashman loves to ballet dance and plays with her brothers — but she needs a special ...

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NICE recommends treatment for people with juvenile idiopathic arthritis

9 September 2021 - NICE has today published final draft guidance which recommends tofacitinib (Xeljanz; Pfizer) as an option for treating ...

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NICE recommends Novartis’ Cosentyx for children with severe psoriasis

3 September 2021 - NICE has recommended Novartis’ interleukin-17A inhibitor Cosentyx (secukinumab) for the treatment of children and young people ...

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Evrysdi (risdiplam) receives CADTH reimbursement recommendation for some patients with spinal muscular atrophy

30 August 2021 - Roche Canada today announced that the CADTH Canadian Drug Expert Committee has issued its final recommendation ...

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