Toddler died of only meningococcal strain not on vaccine program

18 July 2019 - A toddler has died after contracting meningococcal B, the only strain of the potentially deadly disease with ...

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LifeMax receives rare paediatric disease designation for LM-030 for the treatment of Netherton syndrome

18 July 2019 - LifeMax Laboratories today announced that the FDA granted rare paediatric disease designation to LM-030, an investigational therapy ...

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Perth boy battles cystic fibrosis, with a life extending drug frustratingly out of reach

15 July 2019 - In many ways Connor Barrett is just like any other kid - he loves Peppa Pig ...

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LogicBio Therapeutics receives rare paediatric disease designation for LB-001 for the treatment of methylmalonic acidaemia

16 July 2019 -  LogicBio Therapeutics today announced the U.S. FDA has granted rare paediatric disease designation to LB-001, a ...

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Health Canada has authorised Vyvanse (lisdexamphetamine dimesylate), the first and only, chewable tablet for the treatment of attention deficit/hyperactivity disorder

10 July 2019 - Vyvanse offers an additional option for patients who prefer the convenience of a chewable tablet, or who ...

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FDA approves Katerzia, the first and only amlodipine oral suspension for paediatric patients 6 years of age and older

10 July 2019 - Azurity Pharmaceuticals announced today that the U.S. FDA has approved Katerzia (amlodipine) 1 mg/mL oral suspension, ...

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Family to stay in Australia after son with cystic fibrosis initially deemed a 'burden'

8 July 2019 - A Victorian family at risk of being deported back to their homeland of Ireland after their ...

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New treatment for children with type 2 diabetes mellitus

28 June 2019 - EMA’s CHMP has recommended granting an extension of indication to Victoza (liraglutide) to include the treatment of ...

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FDA approves Botox (onabotulinumtoxinA) for paediatric patients with upper limb spasticity

21 June 2019 - Approval marks 10th Botox therapeutic indication in its 30th anniversary year. ...

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FDA expands approval of treatment for cystic fibrosis to include patients ages 6 and older

21 June 2019 - The U.S. FDA today expanded the indication for Symdeko (a combination of tezacaftor/ivacaftor) tablets for treatment of ...

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FDA approves new treatment for paediatric patients with type 2 diabetes

17 June 2019 - The U.S. Food and Drug Administration today approved Victoza (liraglutide) injection for treatment of paediatric patients 10 ...

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FDA grants priority review to Genentech’s Rituxan (rituximab) in children with two rare blood vessel disorders

12 June 2019 - If approved, this would be the first paediatric indication for Rituxan. ...

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Ford government to fund Spinraza, world’s most expensive drug - with age caps

12 June 2019 - The Ford government today announced it will be covering the cost of the drug Spinraza for ...

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PTC Therapeutics receives FDA approval for the expansion of the Emflaza (deflazacort) labeling to include patients 2-5 years of age

7 June 2019 - Emflaza is the only approved treatment for all patients two and over living with Duchenne muscular dystrophy. ...

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Rotorua toddler faces being 'trapped in his own body', parents plead for Spinraza drug funding

5 June 2019 - The last time the Rotorua Daily Post spoke to Rotorua mum Anna Sutherland, her son Heath ...

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