Blog
RSS FeedPosted by Michael Wonder on 18 May 2019
U.S. FDA approves Gattex (teduglutide) for children 1 year of age and older with short bowel syndrome
17 May 2019 - Gattex is the only glucagon-like peptide-2 analogue approved that improves intestinal absorption in patients with SBS who ...
Posted by Michael Wonder on 16 May 2019
FDA approves first anticoagulant (blood thinner) for paediatric patients to treat potentially life-threatening blood clots
16 May 2019 - The U.S. FDA today approved Fragmin (dalteparin sodium) injection, for subcutaneous use, to reduce the recurrence of ...
Posted by Michael Wonder on 08 May 2019
FDA undercuts $375,000 drug in surprise move
8 May 2019 - The US FDA created a workaround this week that effectively undercuts the $375,000 price tag of ...
Posted by Michael Wonder on 07 May 2019
FDA approves first treatment for children with Lambert-Eaton myasthenic syndrome, a rare auto-immune disorder
6 May 2019 - The U.S. FDA today approved Ruzurgi (amifampridine) tablets for the treatment of Lambert-Eaton myasthenic syndrome in patients ...
Posted by Michael Wonder on 06 May 2019
Why one Nova Scotia boy is being treated with drugs that cost $6 million a year despite a better, cheaper alternative
5 May 2019 - Last summer, Health Canada approved a haemophilia drug called Hemlibra that has the potential to change Callum ...
Posted by Michael Wonder on 01 May 2019
FDA approves Kalydeco (ivacaftor) as first and only CFTR modulator to treat eligible infants with CF as early as six months of age
30 April 2019 - Safety data from Phase 3 ARRIVAL study support treatment with Kalydeco in children ages six to <12 ...
Posted by Michael Wonder on 01 May 2019
FDA approves first treatment for all genotypes of hepatitis C in paediatric patients
30 April 2019 - The U.S. FDA today approved Mavyret (glecaprevir and pibrentasvir) tablets to treat all six genotypes of ...
Posted by Michael Wonder on 01 May 2019
Newly approved MS drug to offer relief to children
1 May 2019 - A wonder drug to treat children with multiple sclerosis has been approved for use in Australia. ...
Posted by Michael Wonder on 27 Apr 2019
FDA approves first treatment for paediatric patients with lupus
26 April 2019 - The U.S. FDA today approved Benlysta (belimumab) intravenous infusion for treatment of children with systemic lupus erythematosus ...
Posted by Michael Wonder on 15 Apr 2019
Kiwi father's emotional plea to Jacinda Ardern to fund life saving drug for rare disease
15 April 2019 - The parents of two young girls diagnosed with a rare disease have urged Prime Minister Jacinda ...
Posted by Michael Wonder on 15 Apr 2019
Future in cancer treatment arrives for Australian children and young adults battling leukaemia
15 April 2019 - Hon Greg Hunt MP Minister for Health today announces availability of novel life-saving cancer treatment CAR-T ...
Posted by Michael Wonder on 14 Apr 2019
Saving Charlotte: Bennett to present Parliament with petition calling for funding of SMA drug
14 April 2019 - A 15,000-strong petition calling on PHARMAC to fund a drug to treat spinal muscular atrophy is ...
Posted by Michael Wonder on 11 Apr 2019
Family faces deportation from Australia after son diagnosed with cystic fibrosis
10 April 2019 - Anthony and Christine Hyde's application for permanent residence in Australia has been rejected - because of their ...
Posted by Michael Wonder on 29 Mar 2019
Batten disease medication Brineura available to Australian children via Life Saving Drugs Program
29 March 2019 - A groundbreaking drug that slows the progression of a rare and fatal childhood illness has been ...
Posted by Michael Wonder on 19 Mar 2019
FDA implements new policies to advance the development of drugs to treat or prevent HIV, including in paediatric patients, as part of efforts to end HIV infection
19 March 2019 - The U.S. FDA today issued two final guidances for industry to help product sponsors understand the ...