U.S. FDA approves Gattex (teduglutide) for children 1 year of age and older with short bowel syndrome

17 May 2019 - Gattex is the only glucagon-like peptide-2 analogue approved that improves intestinal absorption in patients with SBS who ...

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FDA approves first anticoagulant (blood thinner) for paediatric patients to treat potentially life-threatening blood clots

16 May 2019 - The U.S. FDA today approved Fragmin (dalteparin sodium) injection, for subcutaneous use, to reduce the recurrence of ...

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FDA undercuts $375,000 drug in surprise move

8 May 2019 - The US FDA created a workaround this week that effectively undercuts the $375,000 price tag of ...

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FDA approves first treatment for children with Lambert-Eaton myasthenic syndrome, a rare auto-immune disorder

6 May 2019 - The U.S. FDA today approved Ruzurgi (amifampridine) tablets for the treatment of Lambert-Eaton myasthenic syndrome in patients ...

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Why one Nova Scotia boy is being treated with drugs that cost $6 million a year despite a better, cheaper alternative

5 May 2019 - Last summer, Health Canada approved a haemophilia drug called Hemlibra that has the potential to change Callum ...

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FDA approves Kalydeco (ivacaftor) as first and only CFTR modulator to treat eligible infants with CF as early as six months of age

30 April 2019 - Safety data from Phase 3 ARRIVAL study support treatment with Kalydeco in children ages six to <12 ...

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FDA approves first treatment for all genotypes of hepatitis C in paediatric patients

30 April 2019 - The U.S. FDA today approved Mavyret (glecaprevir and pibrentasvir) tablets to treat all six genotypes of ...

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Newly approved MS drug to offer relief to children

1 May 2019 - A wonder drug to treat children with multiple sclerosis has been approved for use in Australia. ...

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FDA approves first treatment for paediatric patients with lupus

26 April 2019 - The U.S. FDA today approved Benlysta (belimumab) intravenous infusion for treatment of children with systemic lupus erythematosus ...

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Kiwi father's emotional plea to Jacinda Ardern to fund life saving drug for rare disease

15 April 2019 - The parents of two young girls diagnosed with a rare disease have urged Prime Minister Jacinda ...

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Future in cancer treatment arrives for Australian children and young adults battling leukaemia

15 April 2019 - Hon Greg Hunt MP Minister for Health today announces availability of novel life-saving cancer treatment CAR-T ...

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Saving Charlotte: Bennett to present Parliament with petition calling for funding of SMA drug

14 April 2019 - A 15,000-strong petition calling on PHARMAC to fund a drug to treat spinal muscular atrophy is ...

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Family faces deportation from Australia after son diagnosed with cystic fibrosis

10 April 2019 - Anthony and Christine Hyde's application for permanent residence in Australia has been rejected - because of their ...

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Batten disease medication Brineura available to Australian children via Life Saving Drugs Program

29 March 2019 - A groundbreaking drug that slows the progression of a rare and fatal childhood illness has been ...

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FDA implements new policies to advance the development of drugs to treat or prevent HIV, including in paediatric patients, as part of efforts to end HIV infection

19 March 2019 - The U.S. FDA today issued two final guidances for industry to help product sponsors understand the ...

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