Ascidian Therapeutics announces fast tracks ACDN-01 in Stargardt disease and other ABCA4 retinopathies

Ascidian Therapeutics

29 January 2024 - Ascidian Therapeutics today announced that the US FDA has granted fast track designation for ACDN-01. 

ACDN-01 is the first ever clinical stage RNA exon editor and the only clinical-stage therapeutic targeting the genetic cause of Stargardt disease.

Read Ascidian Therapeutics press release

Michael Wonder

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Michael Wonder

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US , Gene therapy , Fast track