Posted by Michael Wonder on 23 Oct 2017
NHS to fund gene therapy for 'bubble babies'
23 October 2017 - The NHS will fund gene therapy for the first time, with a £500,000 treatment for “bubble baby syndrome”.
Three babies are born each year with an immune defiency condition which leave them at constant risk of developing life-threatening infections.
If left untreated, infants need to be kept isolated from the outside world, which is why the condition is known as “bubble baby syndrome” and usually die before school age.
