Seelos Therapeutics receives rare paediatric disease designation for SLS-005 (trehalose) in Sanfilippo syndrome

Seelos Therapeutics

15 May 2020 - Seelos Therapeutics today announced it has been granted rare paediatric disease designation for SLS-005 in Sanfilippo syndrome from the U.S. FDA.

Seelos was also recently granted orphan disease designation from the FDA for SLS-005 in Sanfilippo syndrome.

Read Seelos Therapeutics press release

Michael Wonder

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Michael Wonder