Posted by Michael Wonder on 21 Jan 2023
Sources of innovation in gene therapies - approaches to achieving affordable prices
21 January 2023 - Gene therapies are a fast growing area of innovation and potentially hold great promise for clinical care.
Most recently, a new gene therapy, etranacogene dezaparvovec (Hemgenix), was approved by the FDA for use in adults with haemophilia B (factor IX deficiency); the cost of this one time treatment has been estimated at $3.5 million.
