14 May 2024 - PDUFA target action date of 13 November 2024. ...
10 May 2024 - Discounting the cost and effect for health intervention is a controversial topic over the last two decades. ...
6 May 2024 - On Wednesday, Kendric Cromer, a 12 year old boy from a suburb of Washington, became the ...
6 May 2024 - iECURE announced today that it has received fast track designation from the US FDA for ECUR-506, ...
2 May 2024 - RMAT designation follows FDA’s review of available safety and efficacy data from the first three patients dosed ...
23 April 2024 - Gene editing and therapy to replace missing or defective genes is one of the most exciting ...
26 April 2024 - Pfizer announced today that the US FDA has approved Beqvez (fidanacogene elaparvovec-dzkt) for the treatment of adults ...
23 April 2024 - Paper outlines policy reforms and market actions to support innovation and access while managing uncertainty, affordability, ...
18 April 2024 - AB-1002 is being studied for the treatment of adults with non-ischaemic cardiomyopathy and New York Heart Association ...
16 April 2024 - Lexeo Therapeutics today announced the US FDA has granted fast track designation to LX2006, the company’s AAVrh.10hFXN ...
2 April 2024 - Positive, previously disclosed results from the global Phase 1/2 trial demonstrated genetic and phenotypic correction combined ...
1 April 2024 - Exa-cel is the first CRISPR-based gene-edited therapy to be submitted for Health Canada review. ...
1 April 2024 - Site initiations scheduled for April; patient dosing expected to begin in Q2 ,2024. ...
19 March 2024 - Health Canada regulatory decision on tofersen new drug submission expected in early 2025. ...
20 March 2024 - A new gene therapy for the fatal genetic disorder metachromatic leukodystrophy, or MLD, will carry a ...