NICE recommends CSL Behring’s haemophilia B gene therapy Hemgenix

28 June 2024 - NICE has recommended CSL Behring’s haemophilia B gene therapy Hemgenix (etranacogene dezaparvovec) for immediate reimbursement by ...

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Vertex announces extended long-term reimbursement agreement with NHS England for access to cystic fibrosis medicines Kaftrio, Symkevi and Orkambi

20 June 2024 - Agreement includes access to any future licence extensions. ...

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NICE enables access to first treatment that targets the underlying pathophysiology of rare disease X-linked hypophosphataemia in adults

21 June 2024 - Kyowa Kirin is delighted by the decision made today by NICE to recommend Crysvita for the treatment ...

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Quality adjusted life years, quality adjusted life year like measures, or neither? The debate continues.

19 June 2024 - The quality-adjusted life year (QALY) is over 50 years old. Debate about the ethical basis for the ...

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Tafamidis meglumine for the treatment of patients with transthyretin amyloidosis with cardiomyopathy (final guidance)

19 June 2024 - NICE has published final evidence-based recommendations on the use of tafamidis meglumine (Vyndaqel) for the treatment ...

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House dust mite allergen for the treatment of patients with allergic rhinitis and allergic asthma caused by house dust mites (review of TA834)

13 June 2024 - The Department of Health and Social Care has asked NICE to produce guidance on the use ...

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Comparing new medicine availability across Europe

12 June 2024 - Each year, the European Pharmaceutical Industry Association (EFPIA) publishes data comparing the availability of new medicines across ...

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Baricitinib for the treatment of patients with juvenile idiopathic arthritis

13 June 2024 - NICE is unable to make a recommendation on the use in the NHS of baricitinib (Olumiant) for ...

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Pembrolizumab in combination with trastuzumab and chemotherapy for the first-line treatment of patients with locally advanced unresectable or metastatic HER2 positive gastric or gastro-oesophageal junction adenocarcinoma (final guidance)

12 June 2024 - NICE has published evidence-based recommendations on the use of pembrolizumab (Keytruda) in combination with trastuzumab and ...

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Voxelotor for the treatment of patients with haemolytic anaemia caused by sickle cell disease

12 June 2024 - NICE has published final evidence-based recommendations on the use of voxelotor (Oxbryta) for the treatment of ...

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Trifluridine with tipiracil hydrochloride in combination with bevacizumab for the treatment of patients with metastatic colorectal cancer after two systemic treatments

6 June 2024 - The Department of Health and Social Care has asked the NICE to produce guidance on the ...

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Danicopan in combination with ravulizumab or eculizumab for the treatment of patients with paroxysmal nocturnal haemoglobinuria

29 May 2024 - The Department of Health and Social Care has asked NICE to produce guidance on the use ...

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Ivosidenib in combination with azacitidine for the first-line treatment of patients with IDH1 R132 mutation positive acute myeloid leukaemia (final guidance)

5 June 2024 - NICE has published final evidence-based guidance on the use of ivosidenib with azacitidine in the NHS ...

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Nivolumab for the adjuvant treatment of patients 12 years and older with completely resected melanoma at high risk of recurrence

5 June 2024 - NICE is unable to make a recommendation on the use of nivolumab (Opdivo) for the adjuvant treatment ...

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Mounjaro is second obesity drug to be approved for use in England

4 June 2024 - Those with BMI of at least 35 kg.m2 and a co-morbidity can now be prescribed tirzepatide and ...

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