Posted by Michael Wonder on 23 Oct 2023
Life changing gene therapy for babies with spinal muscular atrophy
23 October 2023 - The Australian Government is giving more families access to life changing gene therapy for spinal muscular atrophy through the PBS.
Zolgensma (onasemnogene abeparvovec) has been expanded to treat more babies with genetically diagnosed spinal muscular atrophy who are yet to show any symptoms.
