Posted by Michael Wonder on 05 May 2021
PHARMAC asked to fund drug for children with spinal muscular atrophy after it changes four year old's life
5 May 2021 - Four year old Charlotte Bond couldn’t roll over by herself two years ago.
She has type 2 spinal muscular atrophy, a genetic condition that affects the control of muscle movement and causes a person’s muscles to waste away.
Her family moved to Australia where Spinraza is funded. Because of it, she can now take about 250 steps a day unassisted.
