25 September 2020 - There are several techniques for estimating health state utility values, each of which presents pros and cons ...
18 September 2020 - Akcea Therapeutics UK's Waylivra (volanesorsen), the first and only therapy for Familial Chylomicronaemia Syndrome (FCS), will ...
5 March 2020 - An 11-year-old girl with the rare disease phenylketonuria has lost a legal battle in the High ...
24 October 2019 - NHS England has announced a definitive agreement with Vertex Pharmaceuticals to make all three of their ...
17 September 2019 - NHS England is “committed to exploring and developing alternative routes” to enable people with cystic fibrosis ...
11 September 2019 - Families of children with a rare degenerative disease have won their fight for funding for NHS ...
11 September 2019 - It is estimated that in the UK there are around 30 to 50 children living with the ...
17 June 2019 - Proposes three point plan to work round impasse. ...
10 June 2019 - A debate is due to take place in Westminster about a drug for people living with ...
11 June 2019 - MPs call for radical solutions as deadlock remains. ...
5 June 2019 - Stalemate in NHS talks over Orkambi leads parents to buy generic version from Argentina. ...
24 May 2019 - Vertex resisting real-world data proposal. ...
17 May 2019 - Theresa May last night urged US makers of a drug that prolongs life for cystic fibrosis sufferers ...
16 May 2019 - Calls for NHS access to potentially life-saving drugs are growing, one year to the day after ...
11 May 2019 - A number of MPs are calling on a drug company to make a "life-changing" treatment affordable ...