Blog
RSS FeedPosted by Michael Wonder on 14 Jan 2020
B.C. funding decision on pricey drug leaves teen with rare disease facing 'scary' future
13 January 2020 - Miles Ambridge just misses cut-off age to access Spinraza, a potentially life-changing treatment. ...
Posted by Michael Wonder on 09 Jan 2020
New CADTH process for cell and gene therapies
9 January 2020 - CADTH has undertaken an internal review of our processes for drugs and devices, and established a revised ...
Posted by Michael Wonder on 06 Jan 2020
Canadian parents of babies with rare deadly disease look to Novartis treatment lottery
5 January 2020 - Canadian babies with a rare and often fatal muscle-wasting disease may soon have access to a ...
Posted by Michael Wonder on 04 Jan 2020
NICE refuses Akcea’s Waylivra
3 January 2020 - NICE has issued an Evaluation Consultation Document, refusing Waylivra (volanesorsen) as a treatment for familial chylomicronaemia ...
Posted by Michael Wonder on 02 Jan 2020
Toronto parents of baby needing $2.8 million drug turn to Swiss drug maker's dose lottery as a last resort
31 December 2019 - Critics call on Ottawa to improve access to expensive drugs that treat rare diseases. ...
Posted by Michael Wonder on 19 Dec 2019
'Healthy lottery' fears as Novartis plans to give away world’s most expensive drug
19 December 2019 - Novartis aims to give away 100 doses of its $US2.1 million-per-patient ($3.05 million) Zolgensma for spinal ...
Posted by Michael Wonder on 17 Dec 2019
Spinraza funding application reviewed by the Rare Disorders Subcommittee
17 December 2019 - PHARMAC has published the Rare Disorders Subcommittee meeting records which recommends Spinraza (nusinersen), a medication for ...
Posted by Michael Wonder on 10 Dec 2019
Biotech companies defend prices of one-off gene therapy
9 December 2019 - Latest treatments with price tags as high as $2 million require new financing models. ...
Posted by Michael Wonder on 02 Dec 2019
Family asking for help to purchase 'the most expensive drug in the world'
1 December 2019 - Ricardo Batista is desperately hoping for a cure for SMA, for his daughter Eva. ...
Posted by Michael Wonder on 22 Nov 2019
Revised process for cell and gene therapies
21 November 2019 - CADTH has undertaken an internal review and established a novel process for the review of cell and ...
Posted by Michael Wonder on 05 Nov 2019
Talking with Tama, a sick toddler who can't access the drug he needs
5 November 2019 - "Hi!" a bright young voice says down the phone. ...
Posted by Michael Wonder on 03 Nov 2019
Tama is deteriorating fast. But the drug that can help him is too expensive.
31 October 2019 - Tama Hubbard has good days and bad days, just like any other 3-year-old child. ...
Posted by Michael Wonder on 01 Nov 2019
'Why won’t they help him?': 'Broken' mother pleads for PHARMAC funding for toddler's rare disorder
1 November 2019 - The mother of a young boy is pleading with PHARMAC to fund a drug that could ...
Posted by Michael Wonder on 17 Oct 2019
Canadian breakthrough that became the world's most expensive drug, then vanished, gets second chance
17 October 2019 - CBC story about how pharmaceutical industry abandoned gene therapy Glybera sparks NRC effort to re-invent it. ...
Posted by Michael Wonder on 10 Oct 2019
'I'm not ready to bring her back' - NZ not safe for three-year-old with motor neuron disease, mum says
10 October 2019 - Three-year-old New Zealander Charlotte Bond is showing signs she may walk again on her own with ...